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Tag: eteplirsen

Debunking pseudoscience

Eteplirsen and the rise of patient participation in FDA drug approvals.

A long road traveled Let me first preface this article with the admission that the FDA drug approval process is not, or anywhere near perfect.  Also, I do feel conflicted as DMD is a devastating disease with little to no treatment.  I do feel for the children, and their family, who are desperately searching for…
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